Hodgkins Lymphoma: The Hazards of Success
Joseph M. Connors
Journal of Clinical Oncology , Vol 21, Issue 18 (September),
2003: 3388-3390
Chairman, Lymphoma Tumor Group, Clinical Professor, Division of Medical
Oncology, University of British Columbia and the British Columbia, Cancer Agency,
Vancouver, British Columbia, Canada
In line with the theme of carefully identifying and characterizing late
toxicities in the hope of finding strategies to reduce or eliminate them, two
studies in this issue of the Journal of Clinical Oncology address the
late consequences of effective intervention for Hodgkins lymphoma. In the
first of the two studies, Aleman from the Netherlands Cancer Institute
and the Dr Daniel den Hoed Cancer Centre examined the long-term mortality
of 1,261 patients who were 40 years or younger at the time of diagnosis of
Hodgkins lymphoma, treated at their institutions between 1965 and 1987.
With a minimum potential follow-up of more than 15 years, these data provide
some of the most mature results available anywhere in the medical literature.
A key observation from this study was the fact that 55% of the
534 deaths were due to Hodgkins lymphoma, documenting in their
experience that failure to cure the disease, and resultant death from the
lymphoma, remains the greatest single threat to the well-being of patients with
Hodgkins lymphoma. However, the cause of the
excess risk of death switched from Hodgkins lymphoma during the first 10
years after diagnosis to secondary cancers and cardiovascular disease beyond
that. Indeed, the risk of death from Hodgkins lymphoma became negligible
after 20 years. However, the excess deaths from other causes, with
approximately two-thirds being from secondary cancers and one-third from
cardiovascular disease, still lingered more than 30 years from diagnosis. In
keeping with ones intuition, requiring a second course of treatment
because of relapse of Hodgkins disease was strongly associated with an
increased risk of death from secondary cancers, especially solid tumors. Finally,
and perhaps most intriguing, was that the greatest excess risk from these
causes of death other than Hodgkins lymphoma was seen in the youngest
patients, those below the age of 21 years at diagnosis.
Some aspects of this important study are crucially relevant to its
interpretation, indicating that it is primarily of historical interest.
Overall, almost all patients (more than 97%) included in this study received
radiation that most likely consisted of mantle or even more extended fields of
treatment. Although details of the chemotherapy are not provided, it is quite
likely that most patients received regimens that included the agents in
MOPP-type combinations. Very few of the patients accounted for in this study
received secondary treatment with high-dose chemotherapy and stem cell
transplantation because that technique became broadly available only after the
mid 1980s. Most importantly, the treatment technique for
delivery of the radiation to 70% of the patients in the study was abandoned
after the 1970s. Only in retrospect was it appreciated that this
approach was associated with an increased risk of cardiovascular disease. Thus,
although the results of this study remain of considerable interest, it must be
remembered that the observations are based on the long-term effects of
therapeutic approaches that are no longer used. One must especially keep in mind that considerably wider fields of radiation were
given to a much larger proportion of the patients than would be considered
optimal practice today, and the chemotherapy employed has been largely replaced
by less leukemogenic and possibly less carcinogenic regimens such as doxorubicin,
bleomycin, vinblastine and dacarbazine (ABVD).
The second study, by Josting from the German Hodgkins Lymphoma Study
Group, documents the remarkable research program into the treatment of
Hodgkins lymphoma that this group has been able to undertake during the
past two decades. An extraordinary 5,411 patients were entered onto prospective
clinical trials, an effort unequaled elsewhere in the world. With these large
numbers, even relatively uncommon events can be examined. In particular,
this study has focused on the incidence of secondary acute
leukemia and myelodysplastic syndrome and the consequences of the
development of these most serious complications of treatment. They show that
cases of such secondary hematologic disease have been observed in widely
varying patient groups regardless of specific treatment, stage of disease or
age at treatment, with an overall risk of this complication
for the entire group of approximately 1%. The outcome for patients
who developed secondary leukemia or myelodysplasia was quite disappointing,
with freedom from treatment failure falling to 2% and overall survival to 8%
at 2 years. Eighty-five percent of patients had died within 1 year of
documentation of this complication.
While the observation that the treatment of secondary leukemia or
myelodysplasia is largely ineffective is solidly documented by this important
study, certain other points must be interpreted cautiously. Both the Aleman and
Jostinget al studies confirm the observation that almost all cases of leukemia
or myelodysplasia after treatment for Hodgkins lymphoma are
seen in the first decade of followup. However, it is not until that decade has
fully passed that the overall impact of this complication becomes clear. Hence,
there is need for caution interpreting the study by Josting et al, because of
shorter follow-up in the groups of greatest interest. While some of the
observations concerning radiation alone, ABVD, and cyclophosphamide, vincristine,
procarbazine and prednisone (COPP) plus ABVD are mature enough to be solidly
believable, with median follow-up between 7 and 10 years, all of the
observations concerning the BEACOPP regimens are still tentative, with median
follow-up only slightly longer than 3 years. It is important to remember that
escalated BEACOPP incorporates dose-intense alkylating agents, procarbazine,
hematopoietic growth factors (with the potential to stimulate cell division
coincident with exposure to the carcinogenic agents), and radiation for most
patients. Any complete assessment of the potential for such treatment to
induce leukemia or myelodysplasia and the magnitude of this associated risk
must await considerably longer follow-up.
What are the most important lessons that we can
take from these two landmark studies focusing on the late complications of
effective treatment for Hodgkins lymphoma? From the study by Aleman we
have solid confirmation that the use of extended field
radiation is strongly linked to the development of both secondary cancers and
cardiovascular disease, and that these two effects linger in excess of three
decades. However, it is important to maintain some perspective on
relative risks for these patients. Of the excess deaths that occurred, more
than twice as many more were due to Hodgkins lymphoma than to
secondary cancers, and five and a half times as many excess deaths were due to
Hodgkins lymphoma as to cardiovascular disease. In addition, it is clear
that the single most productive maneuver for reducing overall excess deaths
must remain improvement in the effectiveness of the primary treatment. Indeed,
such improvements, if achieved without dramatic intensification of the
treatment, should provide the twin benefits of reduction of excess deaths from
Hodgkins lymphoma and, in addition, reduction of excess deaths from
secondary cancers by avoidance of the negative impact of requiring secondary
treatment. Some documentation of achievement of the first goal is already
provided by the data from Aleman et al. The 20-year disease-specific survival
results show that in the earliest era from 1965 to 1972, risk of death from
Hodgkins lymphoma was approximately 35%, which fell to 13% from 1980 to
1987. We can also hope that other changes already widely adopted in the
treatment of Hodgkins lymphoma will result in fewer nonlymphoma related
excess deaths. Most clinicians have abandoned
MOPP-based chemotherapy in favor of regimens such as ABVD, which carry a lower
risk of inducing leukemia and myelodysplasia while
at the same time improving cure rates from the primary course of chemotherapy.
Outside of clinical trials, most clinicians now use
substantially reduced radiation fields for the typical patient with
Hodgkins lymphoma. It is reasonable to hope that such
reductions in the physical extent of the radiation, coupled with improved
dosimetry and radiation delivery, will further reduce excess deaths from nonlymphoma-related
causes. The question as to whether the potential therapeutic gains of moving to
more intensified regimens such as escalated BEACOPP or Stanford V might not be
counterbalanced by the negative effects of the intensified chemotherapy and
radiation for most patients can only be answered through longer follow-up
of completed and ongoing clinical trials. An alarming trend
is already obvious in the data from Josting with a four- to six-fold
increase in the incidence of secondary leukemia or myelodysplasia as one moves
from radiation or ABVD, for which we have mature follow-up, to escalated
BEACOPP, for which the follow-up is still unfolding.
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